Category : Search result: GALR1 gene variant


Baby's First Steps After Pioneering Gene-Editing Therapy

A 16-month-old boy, KJ Muldoon, takes his first steps after receiving a first-ever personalized CRISPR therapy for a rare genetic disorder at Children's Hospital of Philadelphia. A medical miracle just in time for Christmas.

CRISPR Therapy Paused After Patient Liver Reaction

In a significant setback for gene editing medicine, Intellia Therapeutics halts its Phase 3 ATTR trial following a serious liver adverse event in a patient receiving CRISPR-based treatment NZ-1.

India Regulates Gene Therapy: New Patient Safety Rules

India's health ministry introduces strict new regulations for gene therapy and stem cell treatments, aiming to curb unproven medical procedures while advancing legitimate research for conditions like cancer and rare diseases.

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